BridgeBio Advances Therapy for Limb-Girdle Muscular Dystrophy that Started with Two Patient Families
RARECast - Podcast autorstwa RARECast - Czwartki
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Doug Sproule, chief medical officer of ML Bio Solutions, discusses limb girdle muscular dystrophy type 2i, the company’s experimental therapy to treat the condition, and the power of rare disease patient families to shape drug development.
