RARECast

548 Odcinki

1. Addressing the Delivery Challenges of Genetic Medicines

   Opublikowany: 19.08.2021
2. Targeting Tissues Throughout the Body with RNA Therapies

   Opublikowany: 12.08.2021
3. Delivering Rare Disease Therapies to Patients in Need

   Opublikowany: 5.08.2021
4. An Advocate's Journey through Diagnosis, Loss, and Hope

   Opublikowany: 29.07.2021
5. Using Model Systems to Find Drugs to Repurpose for Rare Diseases

   Opublikowany: 22.07.2021
6. How a Small and Young Foundation Catalyzed Research into a Rare Disease

   Opublikowany: 16.07.2021
7. Overcoming the Limitations of Conventional Cell Engineering

   Opublikowany: 8.07.2021
8. Experimental Therapy for Rare Endocrine Disorder Offers Hope of Improved Care

   Opublikowany: 2.07.2021
9. Forging Gene Therapy Capacity and a Pipeline at the Same Time

   Opublikowany: 24.06.2021
10. Using A Natural DNA Repair Process to Improve Genetic Medicines

    Opublikowany: 18.06.2021
11. Empowering Rare Disease Patients with their Own Health Records

    Opublikowany: 10.06.2021
12. Targeting CNS Disease with Gene Therapies

    Opublikowany: 3.06.2021
13. A New Therapy Offers A Different Approach to Inhibiting the Complement System

    Opublikowany: 28.05.2021
14. Bringing Aberrant Proteins Back into the Fold

    Opublikowany: 20.05.2021
15. A Cat who Curates Rare Mice

    Opublikowany: 13.05.2021
16. Putting the Patient at the Center of Rare Disease Clinical Trials

    Opublikowany: 6.05.2021
17. Creating a Toolkit to Accelerate the Development of Gene Editing Therapies

    Opublikowany: 29.04.2021
18. PTC Looks to Advanced Therapies

    Opublikowany: 22.04.2021
19. Going to Extreme Lengths

    Opublikowany: 15.04.2021
20. Everything’s up to Date in Kansas City, at Least When It Comes to Genomics

    Opublikowany: 8.04.2021