RARECast

548 Odcinki

1. Shortening the Diagnostic Odyssey

   Opublikowany: 1.05.2019
2. Eliminating Barriers to Adoption of Children with Rare Diseases

   Opublikowany: 24.04.2019
3. A Young Rare Disease Advocate Discusses Life with an Undiagnosed Condition

   Opublikowany: 17.04.2019
4. The Benefits of an Open-Source Registry for Rare Diseases

   Opublikowany: 10.04.2019
5. How a Patient Group Helped Drive Drug Development in Rett Syndrome

   Opublikowany: 3.04.2019
6. How Misperceptions Can Create Barriers to Care

   Opublikowany: 27.03.2019
7. Targeting Repeat Expansion Disorders with Next-Gen Antisense Drugs

   Opublikowany: 21.03.2019
8. Getting Misfolding Proteins to Shape Up

   Opublikowany: 13.03.2019
9. A Different Approach to Inhibiting the Complement System

   Opublikowany: 6.03.2019
10. Looking Back in Time to Find Rare Disease Patients Today

    Opublikowany: 27.02.2019
11. Ionis CEO Stanley Crooke Discusses Success as a Platform Technology Company

    Opublikowany: 20.02.2019
12. Orchard Looks toward Harvesting Expanded Gene Therapy Pipeline

    Opublikowany: 13.02.2019
13. Connecting Rare Disease Patients in India and the United States

    Opublikowany: 6.02.2019
14. Regenerative Medicine Moves into the Spotlight

    Opublikowany: 30.01.2019
15. Learning New Tricks from Pathogenic Bacteria to Target the Microbiome

    Opublikowany: 24.01.2019
16. Orphan Drug Accelerator Spin-Out Tackles Rare Endocrine Disorders

    Opublikowany: 16.01.2019
17. Aspa Therapeutics Forges Gene Therapy for Rare Neurological Condition

    Opublikowany: 9.01.2019
18. How Patient-Led Collaborations Are Transforming Rare Disease Drug Discovery and Development

    Opublikowany: 2.01.2019
19. Sobi Expands Its Immunology Franchise with HLH Drug Approval

    Opublikowany: 27.12.2018
20. Learning to Thrive

    Opublikowany: 19.12.2018