RARECast

548 Odcinki

1. Deriving Rare Disease Therapies from Human Plasma

   Opublikowany: 18.10.2017
2. Learning to Live with Purpose

   Opublikowany: 11.10.2017
3. A Mother's Race to Find a Treatment for Her Daughter's Ultra-Rare Condition

   Opublikowany: 4.10.2017
4. Screening for Rare Diseases

   Opublikowany: 27.09.2017
5. A Look at the Changing World of Work for People with a Chronic Illness

   Opublikowany: 20.09.2017
6. Aligning Interests in Rare Disease Partnerships

   Opublikowany: 13.09.2017
7. A Veteran Venture Capitalist Discusses Investing in Rare Disease Drug Development

   Opublikowany: 6.09.2017
8. A Patient Group Crafts Guidelines for Working with Pharma

   Opublikowany: 30.08.2017
9. Bringing Innovation to Business Models for Rare Disease Drug Development

   Opublikowany: 23.08.2017
10. Rethinking Accessibility and Dependency

    Opublikowany: 16.08.2017
11. How Simon Wheatcroft, Blinded by a Rare Disease, Became an Ultramarathoner

    Opublikowany: 9.08.2017
12. Spark Hoping Its Luxturna Will Become First FDA-Approved Gene Therapy

    Opublikowany: 2.08.2017
13. What Rare Patient-Investors Can Learn From Venture Capitalists

    Opublikowany: 26.07.2017
14. Novel Effort Delivers Failed DMD Drug to Former Clinical Trial Participants

    Opublikowany: 19.07.2017
15. Centogene Seeks to Deliver Diagnoses to Rare Disease Patients Early

    Opublikowany: 12.07.2017
16. Albireo Advances Pipeline for Rare Liver and Gastrointestinal Diseases

    Opublikowany: 5.07.2017
17. aTyr Pharma Seeks to Modulate Activity in FSHD and Other Rare Disease

    Opublikowany: 28.06.2017
18. Summit Pursues A Different Approach to Treating Duchenne

    Opublikowany: 21.06.2017
19. Delivering Enzyme Replacement Therapies Across the Blood-Brain Barrier

    Opublikowany: 14.06.2017
20. Sangamo Advances Gene Editing Therapies for Multiple Rare Diseases into the Clinic

    Opublikowany: 7.06.2017