RARECast

548 Odcinki

1. Bridging the Gap Between Basic and Commercial Research for Rare Disease

   Opublikowany: 26.05.2022
2. Stoking Functional Copies of Genes to Compensate for Mutated Ones

   Opublikowany: 19.05.2022
3. Targeting ALS with Synergistic Combinations of Therapies

   Opublikowany: 13.05.2022
4. How a Polish Rare Disease Organizations Is Helping Its Ukrainian Neighbors

   Opublikowany: 5.05.2022
5. Powering a New Era of Genetic Medicine

   Opublikowany: 28.04.2022
6. Searching for a Diagnosis

   Opublikowany: 21.04.2022
7. A Novel Way to Deliver Rare Disease Therapies

   Opublikowany: 14.04.2022
8. Bringing Diversity, Equity, and Inclusion to the Books We Read

   Opublikowany: 7.04.2022
9. From Mila to Millions: Scaling N of 1 Therapies

   Opublikowany: 31.03.2022
10. Genetically Modifying Patients’ Skin Cells to Treat Rare Diseases

    Opublikowany: 24.03.2022
11. Targeting Rare, Immunologic Disorders

    Opublikowany: 18.03.2022
12. Harnessing a Natural Mechanism to Silence Disease

    Opublikowany: 10.03.2022
13. Advancing Precision Medicine with Patient Data

    Opublikowany: 3.03.2022
14. Pregnancy and Motherhood for a Woman with SMA

    Opublikowany: 24.02.2022
15. Steps to Improve Data Gathering of Rare Diseases

    Opublikowany: 17.02.2022
16. Rare Patients Learn to Make Their Voices Heard

    Opublikowany: 10.02.2022
17. Empowering Patient Organizations with Real-World Data

    Opublikowany: 4.02.2022
18. A Healthcare Communications Student Gets an Education as a Patient

    Opublikowany: 27.01.2022
19. Expanding the CRISPR Toolkit

    Opublikowany: 21.01.2022
20. Marrying Antibodies to RNA Therapies to Target Previously Inaccessible Tissues and Cells

    Opublikowany: 13.01.2022