RARECast

548 Odcinki

1. Enabling On-Demand Therapies

   Opublikowany: 16.09.2024
2. After Driving an N-of-1 Therapy for Her Son, an Advocate Turns to Helping Others

   Opublikowany: 5.09.2024
3. Putting Rare Disease Organization in the Business of Drug Development

   Opublikowany: 29.08.2024
4. Understanding the Many Questions Gene Therapies Raise

   Opublikowany: 22.08.2024
5. A Test to Identify People Likely to Develop ALS

   Opublikowany: 15.08.2024
6. How an Ultra-Rare Disease Patient Foundation Advanced a Gene Therapy

   Opublikowany: 8.08.2024
7. Making the $10 Genome a Reality

   Opublikowany: 1.08.2024
8. A No-Nonsense Effort to Develop a Therapy that Works Across Genetic Diseases

   Opublikowany: 25.07.2024
9. Mapping a Perilous Journey with Humor

   Opublikowany: 18.07.2024
10. Restoring Vision in Inherited Retinal Disease

    Opublikowany: 11.07.2024
11. Bringing Genome Sequencing to Rural Populations

    Opublikowany: 4.07.2024
12. Addressing a Blind Spot in Treatments for the Cornea

    Opublikowany: 27.06.2024
13. Taking a Different Approach to Rare Epilepsies

    Opublikowany: 20.06.2024
14. A Rare Disease Drug Developer Tries to Earn Its Stripes

    Opublikowany: 13.06.2024
15. Using Plasma to Treat Rare Diseases

    Opublikowany: 6.06.2024
16. Differentiating Gene Therapies through Regulatory Elements

    Opublikowany: 30.05.2024
17. How One Patient Organization Leverages Research Investments

    Opublikowany: 23.05.2024
18. Charging into the Storm

    Opublikowany: 16.05.2024
19. A Gene Therapy Developer that Embraces Different Models for Reaching Patients

    Opublikowany: 9.05.2024
20. Using Directed Evolution to Develop New Vectors for Genetic Medicines

    Opublikowany: 2.05.2024