RARECast

548 Odcinki

1. Addressing a Shortage of Genetic Counselors with AI

   Opublikowany: 25.04.2024
2. A Small Molecule Therapy to Regenerate Muscle in People with DMD

   Opublikowany: 18.04.2024
3. Forging a Faster Path for Gene Therapies

   Opublikowany: 11.04.2024
4. Determining the Value of Rare Disease Therapies

   Opublikowany: 4.04.2024
5. Buying and Building a Gene Therapy Presence

   Opublikowany: 28.03.2024
6. A Clinical Trial Failure Derails a Promising Technology

   Opublikowany: 21.03.2024
7. Helping People with Undiagnosed Rare Diseases Find Answers

   Opublikowany: 14.03.2024
8. Speeding and Scaling the Development of Genome Editing Therapies

   Opublikowany: 7.03.2024
9. Getting a Next-Generation Genome Editing Therapy for Sickle Cell Disease Back on Track

   Opublikowany: 29.02.2024
10. Trying to Break a Leg in a Wheelchair

    Opublikowany: 22.02.2024
11. A Drug Developer that Makes Pediatric Cancers a Priority

    Opublikowany: 15.02.2024
12. Harnessing the Body’s Natural RNA Machinery to Treat Diseases

    Opublikowany: 8.02.2024
13. Targeting the Leading Cause of Death in Friedreich’s Ataxia with a Gene Therapy

    Opublikowany: 1.02.2024
14. How Inhaled mRNA May Help Rare Disease Patients Breathe Easier

    Opublikowany: 25.01.2024
15. Changing What’s Possible with Cell and Gene Therapies

    Opublikowany: 18.01.2024
16. Why Flying with a Wheelchair Is a Civil Rights Issue

    Opublikowany: 11.01.2024
17. Mapping Spheres of Influence

    Opublikowany: 4.01.2024
18. Bringing Precision to the Treatment of Rare Cancers

    Opublikowany: 28.12.2023
19. The Challenges of Developing a Therapy for Pregnant Women with A Rare Condition

    Opublikowany: 21.12.2023
20. How One Drug Developer Is Addressing Health Inequities

    Opublikowany: 14.12.2023