RARECast

548 Odcinki

1. Accelerating the Development of Genetic Medicines with AI

   Opublikowany: 7.12.2023
2. Leveraging AI to Address the Neuropsychiatric Conditions Associated with a Rare Disease

   Opublikowany: 30.11.2023
3. In Pursuit of a Treatment for His Son, A Lawyer Becomes a Biotech Executive

   Opublikowany: 22.11.2023
4. In Push for Treatment, a Patient Organization Becomes a Trial Sponsor

   Opublikowany: 16.11.2023
5. Delayed Diagnosis of Rare Diseases Takes Staggering Economic Toll

   Opublikowany: 9.11.2023
6. A Cell Therapy to Control Heart-Damaging Inflammation in Duchenne

   Opublikowany: 2.11.2023
7. Stimulating the Growth of Muscle Mass in People with Neuromuscular Diseases

   Opublikowany: 26.10.2023
8. Turning Grief into Action

   Opublikowany: 19.10.2023
9. A Plea to the FDA to Give an Ultra-Rare Disease Drug a Fair Hearing

   Opublikowany: 12.10.2023
10. How the Woolly Mammoth Beat a Path to Better Gene Therapies

    Opublikowany: 5.10.2023
11. A Genetic Counselor’s Journey into Patient Advocacy

    Opublikowany: 28.09.2023
12. A Company in the Fold of Rare Disease

    Opublikowany: 21.09.2023
13. Disabling Antibodies that Drive Rare, Immunological Conditions

    Opublikowany: 14.09.2023
14. Keeping the Sentinels of the Brain Vigilant

    Opublikowany: 7.09.2023
15. Considering the Unfinished Work in Cystic Fibrosis

    Opublikowany: 31.08.2023
16. How to Advocate for Yourself as You Battle Cancer

    Opublikowany: 24.08.2023
17. Targeting Neuroinflammation to Treat ALS

    Opublikowany: 17.08.2023
18. Leveraging Community Partnerships to Address a Rare Disease Behind a Medical Mystery in New Mexico

    Opublikowany: 10.08.2023
19. Accelerating Gene Editing Therapies for Rare, Neurological Conditions

    Opublikowany: 3.08.2023
20. Inhibiting Electrical Activity in Rare, Seizure Disorders

    Opublikowany: 27.07.2023